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· · 来源:go资讯

尽管目前全球仅有5000名婴幼儿使用该药,但罕见病药物的高定价模式,叠加长期持续给药的治疗需求,让Vosoritide的商业表现持续走高。2025年,该药销售额达9.27亿美元,同比增长26%,是BioMarin的核心商业化增长引擎。

Фото: Егор Алеев / ТАСС

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They had been living and working aboard the ISS since August and were expected to stay until February. The crew returned on January 15, which was a decision made by NASA's chief health and medical officer. Once the crew had landed, administrator Jared Isaacman said it was a "serious situation" but didn't go into any detail.